Gene Therapy for Galactosemia: Feat. Mandy and Clayton from BridgeBio
Update: 2025-09-17
Description
In this episode of The Galactosemia Podcast, Ryan sits down with Clayton Beard and Mandy Rohrig from BridgeBio to explore the promise and challenges of gene therapy for galactosemia. They break down how gene replacement works, why viruses are used as delivery systems, and what families should know about the current state of research.
To get in touch with Mandy - Amanda.Rohrig@bridgebio.com
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