How Love Combined with Science Leads to Hope for Rare Disease

Update: 2024-10-22

Description

There are over 7000 rare diseases identified in the U.S. alone. Many of these diseases affect children, leaving families desperate for answers. In this episode, we talk with one of those families and the biotech company offering them new hope. We also talk with an expert on policy that has jump-started R&D for rare diseases.

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In Channel

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How Love Combined with Science Leads to Hope for Rare Disease

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2023-12-1226:47

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00:00

How Love Combined with Science Leads to Hope for Rare Disease

Courtney Dion President and Co-founder The Dion Foundation for Children with Rare Disease, Joe Dion Co-founder and Treasurer The Dion Foundation for Children with Rare Disease, Stéphane Degove Co-founder & CEO Atamyo Therapeutics, Jamie Sullivan VP Policy EveryLife Foundation for Rare Diseases

#box-pro-ellipsis-175925980554318{-webkit-line-clamp:2;}How Love Combined with Science Leads to Hope for Rare Disease

How Love Combined with Science Leads to Hope for Rare Disease

Courtney Dion President and Co-founder The Dion Foundation for Children with Rare Disease, Joe Dion Co-founder and Treasurer The Dion Foundation for Children with Rare Disease, Stéphane Degove Co-founder & CEO Atamyo Therapeutics, Jamie Sullivan VP Policy EveryLife Foundation for Rare Diseases

How Love Combined with Science Leads to Hope for Rare Disease