Innovations in Orphan Drugs for Rare Diseases

Update: 2025-11-26

Description

Novel modalities and the regulatory pathways to clear their journey to patients are driving developments in rare disease treatments in 2025. In this episode of the Drug Solutions podcast, Patrick Lavery, editor for Pharmaceutical Technology®, Pharmaceutical Technology EuropeTM, and BioPharm International®, gathers perspectives from three key opinion leaders across the industry about advancements in oncology and other areas, and the increasing role of patients' families in accelerating R&D.

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In Channel

Innovations in Orphan Drugs for Rare Diseases

2025-11-2611:35

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Novel Drug Delivery Approaches: Refining AAV Vector Deliveries

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Equipment Trends for Addressing Production of New Modalities

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Forecasting Pharma’s Future

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Realizing AI’s Potential

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Dosage Forms: Roundtable On Oral Solid Dosage Trends

2024-10-3020:01

Alternative Drug Delivery Methods for Biologics: Where Are We At?

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Meeting Industry Needs: Fill/Finish Advances from a CDMO Perspective

2024-09-1024:28

Growth and Advancements in Fill/Finish

2024-06-2519:19

All About Data: Looking at the EHDS in More Detail

2024-05-2813:14

A Closer Look at mRNA in Oncology and Vaccines

2024-04-3024:12

Applying Appropriate Analytics to Drug Development

2024-03-2624:07

The Biosimilars Landscape

2024-01-3127:58

Staying on Track with Formulation of Cell Culture Media

2023-12-0524:47

Gliding Through the Ins and Outs of the Pharma Supply Chain

2023-11-1421:35

Digital Transformation in the Biopharma Industry

2023-10-1924:07

Starting Up in the CGT Manufacturing Space

2023-10-0525:38

Breaking Through the Barriers of Drug Development

2023-09-0520:27

mRNA Past, Present, and Future

2023-08-1730:37

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Innovations in Orphan Drugs for Rare Diseases

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Innovations in Orphan Drugs for Rare Diseases

Pharm Tech

Innovations in Orphan Drugs for Rare Diseases